EDIT 102
Alternative Names: EDIT-102Latest Information Update: 28 Mar 2024
At a glance
- Originator Editas Medicine
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene modulators; USH2A protein modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Usher syndromes