Research programme: CNS disorders gene therapy - Beacon Therapeutics
Latest Information Update: 28 Mar 2024
At a glance
- Originator Applied Genetic Technologies Corporation
- Developer Beacon Therapeutics
- Class Antidementias; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Amyotrophic lateral sclerosis; Dementia
Most Recent Events
- 28 Mar 2024 No recent reports of development identified for preclinical development in Dementia in USA (Parenteral)
- 28 Mar 2023 No recent reports of development identified for preclinical development in Amyotrophic-lateral-sclerosis in USA (Parenteral)
- 29 Sep 2021 Applied Genetic Technologies plans IND enabling studies for Amyotrophic lateral sclerosis in 2022