BL 001
Alternative Names: BL-001Latest Information Update: 18 Mar 2025
At a glance
- Originator Duke University
- Developer Bloom Science
- Class Antiepileptic drugs; Bacteria; Neuroprotectants; Obesity therapies
- Mechanism of Action GABA modulators; Gastrointestinal microbiome modulators; Glutamate agonists
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Dravet syndrome; Obesity
- Phase 0 Epilepsy
- No development reported Amyotrophic lateral sclerosis