Research programme: RNA targeted small molecules - Arrakis Therapeutics/Roche
Latest Information Update: 28 May 2024
At a glance
- Originator Arrakis Therapeutics
- Class Small molecules
- Mechanism of Action RNA modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Unspecified