ION 253
Alternative Names: ION-253; IONIS-JBI2-2.5RxLatest Information Update: 24 Jan 2023
Price :
$50 *
At a glance
- Originator Ionis Pharmaceuticals
- Developer Ionis Pharmaceuticals; Janssen Biotech
- Class Antisense oligonucleotides
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Gastrointestinal disorders