ION 547
Alternative Names: ION-547Latest Information Update: 29 Mar 2023
At a glance
- Originator Ionis Pharmaceuticals
- Class Antisense oligonucleotides; Cardiovascular therapies
- Mechanism of Action Factor XII inhibitors; Gene silencing
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Discontinued Thrombosis
Most Recent Events
- 10 Mar 2023 Discontinued - Phase-I for Thrombosis (In volunteers) in Canada (SC) before March 2023 (Ionis Pharmaceuticals pipeline, March 2023)
- 14 Sep 2022 Ionis Pharmaceuticals completes a phase I trial in volunteers in Canada (SC) (NCT04934891)
- 04 May 2021 Phase-I clinical trials in Thrombosis (In volunteers) in Canada (SC) (NCT04934891)