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NTLA 2002

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Drug Profile

NTLA 2002

Alternative Names: KLKB1 HAE therapeutic - Intellia Therapeutics; NTLA-2002

Latest Information Update: 29 Jan 2025

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At a glance

  • Originator Intellia Therapeutics
  • Class Gene therapies; Vascular disorder therapies
  • Mechanism of Action Prekallikrein expression inhibitors
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Hereditary angioedema
  • New Molecular Entity No

Highest Development Phases

  • Phase III Hereditary angioedema

Most Recent Events

  • 22 Jan 2025 Intellia Therapeutics announces intention to launch NTLA 2002 for Hereditary angioedema in USA in 2027
  • 24 Oct 2024 Efficacy, adverse events and pharmacodynamics data from a phase I/II trial in Hereditary angioedema presented at the Annual Scientific Meeting of the American College of Allergy, Asthma & Immunology (ACAAI-2024)
  • 24 Oct 2024 Efficacy and adverse event data from a phase I/II trials in Hereditary angioedema released byIntellia Therapeutics

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