QRX 1204
Alternative Names: QRX-1204Latest Information Update: 28 Jan 2024
At a glance
- Originator ProQR Therapeutics
- Class Antisense oligoribonucleotides
- Mechanism of Action Notch-3 receptor modulators; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported CADASIL
Most Recent Events
- 28 Jan 2024 No recent reports of development identified for research development in CADASIL in Netherlands (Parenteral)