TGTX 113
Alternative Names: TGTX-113; TSHA-113Latest Information Update: 28 May 2025
At a glance
- Originator University of Texas Southwestern Medical Center
- Developer Taysha Gene Therapies; University of Texas Southwestern Medical Center
- Class MicroRNAs
- Mechanism of Action Gene expression modulators; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Neurodegenerative disorders
Most Recent Events
- 28 May 2025 No recent reports of development identified for preclinical development in Neurodegenerative-disorders in USA (Intrathecal)
- 31 Dec 2022 Taysha Gene Therapies has patent pending for RNA interference (RNAi) constructs targeting MAPT in-licensed from The Board of Regents of The University of Texas System worldwide
- 15 Apr 2021 Preclinical trials in Neurodegenerative disorders in USA (Intrathecal) before April 2021