Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

DYNE 301

Next Previous
Drug Profile

DYNE 301

Alternative Names: DYNE-301; Facioscapulohumeral muscular dystrophy therapy - Dyne Therapeutics

Latest Information Update: 28 Jul 2025

Price :
$50 *
Note:
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator Dyne Therapeutics
  • Class Antisense oligonucleotides; Drug conjugates; Fab fragments; Immunoconjugates
  • Mechanism of Action DUX4L1 protein expression inhibitors; RNA interference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity Yes

Highest Development Phases

  • No development reported Facioscapulohumeral muscular dystrophy

Most Recent Events

  • 28 Jul 2025 No recent reports of development identified for preclinical development in Facioscapulohumeral-muscular-dystrophy in USA (Parenteral)
  • 13 Oct 2021 Dyne Therapeutics announces intention to submit IND for DYNE 301 in Facioscapulohumeral muscular dystrophy (FSHD) in the second half of 2022
  • 25 Jun 2021 Preclinical trials in Facioscapulohumeral muscular dystrophy in USA (Parenteral)

You need to be a logged in or subscribed to view this content

Request demo (opens in a new window)
If your organization or you do not have a subscription, try one of the following: If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top