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DYNE 301

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Drug Profile

DYNE 301

Alternative Names: DYNE-301; Facioscapulohumeral muscular dystrophy therapy - Dyne Therapeutics

Latest Information Update: 15 Oct 2021

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At a glance

  • Originator Dyne Therapeutics
  • Class Antisense oligonucleotides; Drug conjugates; Fab fragments; Immunoconjugates
  • Mechanism of Action DUX4L1 protein expression inhibitors; RNA interference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity Yes

Highest Development Phases

  • Preclinical Facioscapulohumeral muscular dystrophy

Most Recent Events

  • 13 Oct 2021 Dyne Therapeutics announces intention to submit IND for DYNE 301 in Facioscapulohumeral muscular dystrophy (FSHD) in the second half of 2022
  • 25 Jun 2021 Preclinical trials in Facioscapulohumeral muscular dystrophy in USA (Parenteral)
  • 25 Jun 2021 Preclinical pharmacodynamics data in Facioscapulohumeral muscular dystrophy released by Dyne Therapeutics

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