RAPA 501
Alternative Names: Allogeneic off-the-shelf RAPA-501 cells; Autologous Hybrid T-Cell Therapy - Rapa Therapeutics; Autologous hybrid TREG/Th2 cell therapy; RAPA-501; RAPA-501 Autologous T cells; RAPA-501 T cell therapy; RAPA-501-Allo cellsLatest Information Update: 19 Dec 2023
At a glance
- Originator Rapa Therapeutics
- Class Immunotherapies; T lymphocyte cell therapies
- Mechanism of Action T lymphocyte replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase II/III Amyotrophic lateral sclerosis
- Phase I/II SARS-CoV-2 acute respiratory disease
Most Recent Events
- 13 Dec 2023 Rapa Therapeutics initiates in an expanded access trial for Amyotrophic lateral sclerosis in USA (IV) (NCT06169176)
- 30 Dec 2020 Phase-I/II clinical trials in SARS-COV-2 acute respiratory disease (Late-stage disease) in USA (IV) (NCT04482699)
- 15 Dec 2020 Phase-II/III clinical trials in Amyotrophic lateral sclerosis in USA (IV) (NCT04220190)