CAN 203
Alternative Names: CAN-203Latest Information Update: 09 May 2023
At a glance
- Originator CANbridge Pharmaceuticals; University of Massachusetts Medical School
- Developer CANbridge Pharmaceuticals
- Class Gene therapies
- Mechanism of Action Gene transference; SMN complex protein expression stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Spinal muscular atrophy
Most Recent Events
- 03 May 2023 Pharmacodynamics data from preclinical studies in Spinal muscular atrophy released by CANbridge Pharmaceuticals
- 03 Jan 2023 CANbridge Pharmaceuticals exercised its option to secure the exclusive global rights from UMass Chan Medical School for a novel second-generation gene therapy
- 16 May 2022 Pharmacodynamics data from a preclinical study in Spinal muscular atrophy presented at the annual meeting of the American Society of Gene and Cell Therapy (ASGCT-2022)