Research programme: muscular dystropy gene therapy - 4D Molecular Therapeutics
Latest Information Update: 28 Jul 2024
At a glance
- Originator 4D Molecular Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Duchenne muscular dystrophy