Research programme: enzyme therapeutics - Chiesi Global Rare Diseases
Latest Information Update: 28 Jul 2024
At a glance
- Originator Chiesi Global Rare Diseases
- Class Enzymes
- Mechanism of Action Enzyme replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Lysosomal storage diseases
Most Recent Events
- 28 Jul 2024 No recent reports of development identified for research development in Lysosomal storage diseases in USA (Parenteral)
- 29 Jun 2020 Chiesi Global Rare Diseases in-licenses xB3 TM platform technology from Bioasis Technologies
- 29 Jun 2020 Early research in Lysosomal storage diseases in USA (Parenteral)