Research programme: non-viral gene therapies - Carmine Therapeutics/Takeda Pharmaceutical
Latest Information Update: 18 Oct 2022
Price :
$50 *
At a glance
- Originator Carmine Therapeutics
- Developer Carmine Therapeutics; Takeda
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Lung disorders; Retinal disorders