Research programme: muscular dystrophy therapeutics - Healx/Muscular Dystrophy UK
Latest Information Update: 28 Aug 2024
At a glance
- Originator Healx; Muscular Dystrophy UK
- Developer Healx
- Class
- Mechanism of Action Undefined mechanism
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Facioscapulohumeral muscular dystrophy
Most Recent Events
- 28 Aug 2024 No recent reports of development identified for research development in Facioscapulohumeral-muscular-dystrophy in United Kingdom
- 15 Jul 2020 Healx signs collaborative research agreement with Muscular Dystrophy UK for development of therapeutics in Facioscapulohumeral muscular dystrophy
- 15 Jul 2020 Early research in Facioscapulohumeral muscular dystrophy in United Kingdom (unspecified route)