Research programme: genetic cardiomyopathy therapeutics - MyoKardia/Fulcrum Therapeutics
Latest Information Update: 30 Oct 2025
At a glance
- Originator Fulcrum Therapeutics; MyoKardia
- Class Cardiovascular therapies; Small molecules
- Mechanism of Action Gene expression modulators
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Cardiomyopathies
Most Recent Events
- 30 Oct 2025 Discontinued - Preclinical for Cardiomyopathies in USA (unspecified route)(Bristol-Myers Squibb pipeline, October 2025)(Fulcrum Therapeutics pipeline, October 2025)
- 08 Feb 2023 Preclinical trials in Cardiomyopathies in USA (unspecified route) as of February 2023 (Fulcrum Therapeutics pipeline, February 2023)
- 17 Nov 2020 MyoKardia has been acquired by Bristol-Myers Squibb