Research programme: genetic cardiomyopathy therapeutics - MyoKardia/Fulcrum Therapeutics
Latest Information Update: 10 Feb 2023
At a glance
- Originator Fulcrum Therapeutics; MyoKardia
- Class Cardiovascular therapies; Small molecules
- Mechanism of Action Gene expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Cardiomyopathies
Most Recent Events
- 08 Feb 2023 Preclinical trials in Cardiomyopathies in USA (unspecified route) as of February 2023 (Fulcrum Therapeutics pipeline, February 2023)
- 17 Nov 2020 MyoKardia has been acquired by Bristol-Myers Squibb
- 22 Jul 2020 MyoKardia and Fulcrum Therapeutics agree to co-promote and co-develop therapeutics for genetic cardiomyopathies