Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

FBX 101

Next Previous
Drug Profile

FBX 101

Alternative Names: AAVrh.10-hGALC; AAVrh10-GALC; AAVrh10-GALC - Forge Biologics; AAVrh10.hGALC; FBX-101

Latest Information Update: 21 Mar 2024

Price :
$50 *
Note:
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator University of Pittsburgh
  • Developer Forge Biologics
  • Class Gene therapies
  • Mechanism of Action Galactosylceramidase replacements; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Globoid cell leukodystrophy
  • New Molecular Entity No

Highest Development Phases

  • Phase I/II Globoid cell leukodystrophy

Most Recent Events

  • 20 Mar 2024 FBX 101 receives Innovation Passport designation for globoid cell leukodystrophy in United Kingdom
  • 20 Mar 2024 Efficacy and adverse events data from a phase I/II REKLAIM trial in globoid cell leukodystrophy released by Forge Biologics
  • 23 Feb 2023 Efficacy and adverse events data from a phase-I/II RESKUE trial in Globoid cell leukodystrophy released by Forge Biologics

You need to be a logged in or subscribed to view this content

Request demo (opens in a new window)
If your organization or you do not have a subscription, try one of the following: If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top