VTA 110
Alternative Names: VTA-110Latest Information Update: 28 Aug 2024
At a glance
- Originator Johns Hopkins University; Kennedy Krieger Institute
- Developer Vita Therapeutics
- Class Induced pluripotent stem cell therapies; Stem cell therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Duchenne muscular dystrophy; Limb girdle muscular dystrophies
Most Recent Events
- 28 Aug 2024 No recent reports of development identified for preclinical development in Duchenne muscular dystrophy in USA
- 28 Aug 2024 No recent reports of development identified for research development in Limb-girdle-muscular-dystrophies in USA
- 29 Jul 2020 Early research in Limb girdle muscular dystrophies in USA (unspecified route)