Research programme: Rett Syndrome Therapeutics - Vico Therapeutics
Latest Information Update: 31 Jul 2020
At a glance
- Originator Vico Therapeutics
- Class Antisense oligonucleotides
- Mechanism of Action Methyl-CpG-binding protein 2 expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Rett syndrome