Research programme: muscular dystrophy gene therapies - Cartesian Therapeutics
Alternative Names: muscular dystrophy gene therapies - Sarepta Therapeutics/Cartesian TherapeuticsLatest Information Update: 05 Dec 2023
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At a glance
- Originator Selecta Biosciences
- Developer Sarepta Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Duchenne muscular dystrophy; Limb girdle muscular dystrophies
Most Recent Events
- 13 Jun 2022 Sarepta Therapeutics extends options under the Research License and Option Agreement with Selecta Biosciences for its Duchenne muscular dystrophy (DMD) and certain Limb-girdle muscular dystrophies (LGMDs) gene therapy programme
- 30 May 2021 Preclinical trials in Duchenne muscular dystrophy in USA (Parenteral)
- 30 May 2021 Preclinical trials in Limb girdle muscular dystrophies in USA (Parenteral)