EP 0042 - Ellipses Pharma
Alternative Names: EP0042Latest Information Update: 02 Feb 2025
At a glance
- Originator The Institute of Cancer Research
- Developer Ellipses Pharma
- Class Antineoplastics
- Mechanism of Action Aurora kinase inhibitors; Fms-like tyrosine kinase 3 inhibitors
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Orphan Drug Status
Yes - Acute myeloid leukaemia
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Phase I/II Acute myeloid leukaemia; Chronic myelomonocytic leukaemia; Myelodysplastic syndromes
Most Recent Events
- 07 Dec 2024 Efficacy, pharmacokinetics and adverse event data from a phase I/II trial in Acute myeloid leukemia, Myelodysplastic syndromes and Chronic myelomonocytic leukaemia presented at the 66th American Society of Hematology Annual Meeting and Exposition (ASH-Hem-2024)
- 09 Dec 2023 Updated efficacy and adverse event data from a Acute myeloid leukemia presented at the 65th American Society of Hematology Annual Meeting and Exposition (ASH-2023)
- 14 Mar 2023 EP 0042 - Ellipses Pharma receives Orphan Drug status for Acute myeloid leukaemia in USA