Research programme: neurological disorder therapies - Foundation for Angelman Syndrome Therapeutics/Healx
Latest Information Update: 28 Sep 2024
At a glance
- Originator Foundation for Angelman Syndrome Therapeutics; Healx
- Developer Healx
- Class
- Mechanism of Action Undefined mechanism
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Angelman syndrome
Most Recent Events
- 28 Sep 2024 No recent reports of development identified for research development in Angelman-syndrome in United Kingdom
- 12 Aug 2020 Healx signs collaborative research agreement with Foundation for Angelman Syndrome for development of therapeutics in Angelman syndrome
- 12 Aug 2020 Early research in Angelman syndrome in United Kingdom (unspecified route)