Drug Profile

MDL 101

Alternative Names: MDL-101

Latest Information Update: 07 Oct 2024

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At a glance

Originator Modalis Therapeutics
Class Gene therapies
Mechanism of Action Gene modulators; Gene transference

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity No
Available For Licensing Yes

Highest Development Phases

Preclinical Muscular dystrophies

Most Recent Events

30 Sep 2024 MDL 101 is still in preclinical trials for Muscular dystrophies in Japan
30 Sep 2024 Modalis Therapeutics applies for Orphan Drug status in Muscular dystrophies in USA
30 Sep 2024 US FDA approves Rare Pediatric Disease (RPD) designation for MDL 101 in Muscular dystrophies

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