TSHA 117
Alternative Names: TSHA-117Latest Information Update: 28 Oct 2024
At a glance
- Originator University of Texas Southwestern Medical Center
- Developer Taysha Gene Therapies
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Pervasive child development disorders
Most Recent Events
- 28 Oct 2024 No recent reports of development identified for preclinical development in Pervasive-child-development-disorders in USA
- 07 Sep 2020 Preclinical trials in Pervasive child development disorders in USA (unspecified route) before September 2020 (Taysha Gene Therapies' pipeline, September 2020)