Research programme: gene editing therapies - Moderna Therapeutics/Vertex Pharmaceuticals
Latest Information Update: 29 Feb 2024
At a glance
- Originator Moderna Therapeutics; Vertex Pharmaceuticals
- Class Antifibrotics; Gene therapies; RNA
- Mechanism of Action Gene modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Cystic fibrosis