Research programme: genetic disorder gene therapies - Solid Biosciences
Latest Information Update: 28 Nov 2024
At a glance
- Originator AavantiBio
- Developer Solid Biosciences
- Class Gene therapies
- Mechanism of Action Gene transference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Inborn genetic disorders