Research programme: CNS disorder therapeutics - Bristol Myers Squibb/Insitro
Latest Information Update: 06 Apr 2026
At a glance
- Originator Bristol-Myers Squibb; Insitro
- Class Antidementias; Small molecules
- Mechanism of Action RNA modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Amyotrophic lateral sclerosis
- Discontinued Frontotemporal dementia
Most Recent Events
- 06 Apr 2026 Discontinued for Frontotemporal dementia in USA (unspecified route) prior to April 2026 (Insitro pipeline, April 2026)
- 23 Oct 2025 Research programme: CNS disorder therapeutics is still in research phase for Frontotemporal dementia in USA
- 23 Oct 2025 Research programme: CNS disorder therapeutics is still in research phase for Amyotrophic lateral sclerosis in USA