Sonpiretigene isteparvovec - Nanoscope Therapeutics
Alternative Names: MCO-010; MOGENRY™; vMCO 1; vMCO-010Latest Information Update: 12 Mar 2026
At a glance
- Originator Nanoscope Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Eye protein replacements; Gene transference
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Orphan Drug Status
Yes - Retinal disorders; Stargardt disease; Retinitis pigmentosa
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preregistration Retinitis pigmentosa
- Phase II Stargardt disease
- Preclinical Leber congenital amaurosis
- No development reported Dry age-related macular degeneration
Most Recent Events
- 24 Feb 2026 Nanoscope therapeutics plans a phase III STARGAZE registrational trial for Stargardt disease (Intravitreous) in 2026
- 20 Jan 2026 Sonpiretigene isteparvovec - Nanoscope Therapeutics receives Orphan Drug status for Retinal disorders in Japan
- 20 Jan 2026 Sonpiretigene isteparvovec - Nanoscope Therapeutics receives Sakigake designation for Retinal disorders in Japan