Sonpiretigene isteparvovec - Nanoscope Therapeutics
Alternative Names: MCO-010; vMCO 1; vMCO-010Latest Information Update: 14 Nov 2025
At a glance
- Originator Nanoscope Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Eye protein replacements; Gene transference
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Orphan Drug Status
Yes - Stargardt disease; Retinitis pigmentosa
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preregistration Retinitis pigmentosa
- Phase II Stargardt disease
- No development reported Dry age-related macular degeneration
Most Recent Events
- 04 Nov 2025 Efficacy and adverse events data from a phase I/IIa trial in Retinitis pigmentosa released by Nanoscope thearpeutics
- 02 Sep 2025 Sonpiretigene isteparvovec - Nanoscope Therapeutics receives Regenerative Medicine Advanced Therapy (RMAT) status for Stargardt disease in USA
- 26 Aug 2025 MCO 010 receives orphan designations for non-syndromic dystrophy, syndromic rod-dominant dystrophy, cone-dominant dystrophy and macular dystrophy