Sonpiretigene isteparvovec - Nanoscope Therapeutics
Alternative Names: MCO-010; MOGENRY™; vMCO 1; vMCO-010Latest Information Update: 19 May 2026
At a glance
- Originator Nanoscope Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Eye protein replacements; Gene transference
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Orphan Drug Status
Yes - Retinal disorders; Stargardt disease; Retinal dystrophies; Retinitis pigmentosa
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preregistration Retinitis pigmentosa
- Phase II Stargardt disease
- Preclinical Dry age-related macular degeneration; Leber congenital amaurosis
Most Recent Events
- 30 Mar 2026 Sonpiretigene isteparvovec - Nanoscope Therapeutics receives Orphan Drug status for Retinal dystrophies in European Union
- 30 Mar 2026 Sonpiretigene isteparvovec receives Orphan Drug status for Retinal dystrophies in Saudi Arabia
- 23 Mar 2026 Sonpiretigene isteparvovec is still in preclinical trials for Dry age-related macular degeneration in USA (Intravitreous, Injection)