Sonpiretigene isteparvovec - Nanoscope Therapeutics
Alternative Names: MCO-010; vMCO 1; vMCO-010Latest Information Update: 09 Sep 2025
At a glance
- Originator Nanoscope Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Eye protein replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preregistration Retinitis pigmentosa
- Phase II Stargardt disease
- No development reported Dry age-related macular degeneration
Most Recent Events
- 02 Sep 2025 Sonpiretigene isteparvovec - Nanoscope Therapeutics receives Regenerative Medicine Advanced Therapy (RMAT) status for Stargardt disease in USA
- 26 Aug 2025 MCO 010 receives orphan designations for non-syndromic dystrophy, syndromic rod-dominant dystrophy, cone-dominant dystrophy and macular dystrophy
- 26 Aug 2025 Nanoscope Therapeutics plans a phase II trial for Dry macular degeneration by the end of 2025 (Intravitreous)