Tarperprumig - Alexion Astrazeneca Rare Disease
Alternative Names: ALXN-1820Latest Information Update: 14 Sep 2025
At a glance
- Originator Alexion Pharmaceuticals
- Developer Alexion AstraZeneca Rare Disease
- Class Antianaemics; Bispecific antibodies
- Mechanism of Action Properdin inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Haematological disorders; Sickle cell anaemia
Most Recent Events
- 09 Sep 2025 Alexion Pharmaceuticals plans to initiate a phase II trial for Vasculitis in Argentina, Brazil, Canada, China, France, Germany, Italy, Poland, South Korea, Spain, Taiwan, Turkey and United Kingdom (Parenteral) (NCT07160608)
- 09 Nov 2023 Discontinued - Phase-I for Haematological disorders (In volunteers) in Australia (IV)
- 09 Nov 2023 Discontinued - Phase-I for Haematological disorders (In volunteers) in Australia (SC)