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Elsunersen - Praxis-Precision-Medicines

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Drug Profile

Elsunersen - Praxis-Precision-Medicines

Alternative Names: PRAX-222

Latest Information Update: 13 Aug 2025

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At a glance

  • Originator Praxis Precision Medicines
  • Class Antiepileptic drugs; Antisense oligonucleotides
  • Mechanism of Action Gene silencing; SCN2A protein expression inhibitors
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Epilepsy
  • New Molecular Entity Yes

Highest Development Phases

  • Phase III Epilepsy

Most Recent Events

  • 04 Aug 2025 Phase-III clinical trials in Epilepsy (In adolescents, In children, In neonates, In infants) in USA (Intrathecal) (NCT07019922)
  • 28 Feb 2025 Praxis Precision Medicines plans a registrational EMBRAVE3 trial for Epilepsy in the middle of 2025 (NCT07019922)
  • 13 Jan 2025 Praxis Precision Medicines announced the completion of discussions with global regulatory agencies to harmonize a registrational study design for elsunersen

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