Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

Elsunersen - Praxis-Precision-Medicines

Next Previous
Drug Profile

Elsunersen - Praxis-Precision-Medicines

Alternative Names: PRAX-222

Latest Information Update: 03 Jul 2025

Price :
$50 *
Note:
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator Praxis Precision Medicines
  • Class Antiepileptic drugs; Antisense oligonucleotides
  • Mechanism of Action Gene silencing; SCN2A protein expression inhibitors
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Epilepsy
  • New Molecular Entity Yes

Highest Development Phases

  • Phase I/II Epilepsy

Most Recent Events

  • 28 Feb 2025 Praxis Precision Medicines plans a registrational EMBRAVE3 trial for Epilepsy in the middle of 2025 (NCT07019922)
  • 13 Jan 2025 Praxis Precision Medicines announced the completion of discussions with global regulatory agencies to harmonize a registrational study design for elsunersen
  • 10 Jan 2024 Efficacy data from a phase-I/II EMBRAVE trial in Epilepsy released by Praxis Precision Medicines

You need to be a logged in or subscribed to view this content

Request demo (opens in a new window)
If your organization or you do not have a subscription, try one of the following: If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top