TSHA 120
Alternative Names: TSHA-120Latest Information Update: 21 May 2024
At a glance
- Originator HANNAHS HOPE FUND
- Developer Taysha Gene Therapies
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Giant axonal neuropathy
Most Recent Events
- 01 Jan 2024 Taysha Gene Therapies initiates the transfer of the US FDA IND application and investigational clinical trial material for TSHA 120 in giant axonal neuropathy to NINDS
- 31 Dec 2023 Taysha Gene Therapies has patent protection for method of treatment with an rAAV vector comprising a transgene encoding gigaxonin, including methods of treating giant axonal neuropathy in USA
- 19 Sep 2023 Taysha announces that Astellas Gene Therapies elects not to exercise its option to obtain an exclusive license to TSHA120 under the agreement