BMN 255
Alternative Names: BMN-255Latest Information Update: 02 May 2024
At a glance
- Originator BioMarin Pharmaceutical
- Class Small molecules; Urologics
- Mechanism of Action Glycollate oxidase inhibitors
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Hyperoxaluria
Most Recent Events
- 24 Apr 2024 Discontinued - Phase-II for Hyperoxaluria (PO), due to portfolio prioritization
- 12 Sep 2023 Phase-II clinical trials in Hyperoxaluria (PO) (BioMarin Pharmaceuticals pipeline, September 2023)
- 07 Sep 2023 BioMarin Pharmaceutical plans a clinical trial for hyperoxaluria in non-alcoholic fatty liver disease