M 011
Alternative Names: GBAM6P; M-011Latest Information Update: 28 Feb 2025
At a glance
- Originator M6P Therapeutics
- Class Enzymes; Recombinant proteins
- Mechanism of Action Enzyme replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- No development reported Gaucher's disease
Most Recent Events
- 28 Feb 2025 No recent reports of development identified for preclinical development in Gaucher's-disease in USA
- 09 Feb 2023 M6P Therapeutics plans to submit IND in Gaucher's disease by Q1 2023 (M6P Therapeutics website, February 2023)
- 10 Feb 2022 Pharmacodynamics data from preclinical trial presented at the 18th Annual WORLDSymposium™ (Annual WORLDSymposium-2022)