M 031
Alternative Names: GalCM6P; M-031Latest Information Update: 12 Apr 2023
Price :
$50 *
At a glance
- Originator M6P Therapeutics
- Class Enzymes; Recombinant proteins
- Mechanism of Action Enzyme replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Discontinued Globoid cell leukodystrophy
Most Recent Events
- 12 Apr 2023 Discontinued - Preclinical for Globoid cell leukodystrophy in USA (unspecified route) (M6P Therapeutics pipeline, April 2023)
- 04 Feb 2021 M 031 is available for licensing as of 04 Feb 2021
- 28 Jan 2021 Recombinant enzyme replacement therapies received rare paediatric disease designations for Lysosomal storage diseases in USA