M 0X4
Alternative Names: M-0X4; Non-viral gene TxLatest Information Update: 21 Jul 2021
At a glance
- Originator M6P Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- Research Lysosomal storage diseases