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Drug Profile

M 053

Alternative Names: Lenti-GLA-S1S3; M-053

Latest Information Update: 12 Apr 2023

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At a glance

Originator M6P Therapeutics
Class Gene therapies
Mechanism of Action Alpha-galactosidase replacements; Gene transference

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity No
Available For Licensing Yes

Highest Development Phases

Discontinued Fabry's disease

Most Recent Events

12 Apr 2023 Discontinued - Preclinical for Fabry's disease in USA (Parenteral) (M6P Therapeutics pipeline, April 2023)
04 Feb 2021 M 053 is available for licensing as of 04 Feb 2021
04 Feb 2021 Preclinical trials in Fabry's disease in USA (Parenteral)

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