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M 052

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Drug Profile

M 052

Alternative Names: AAV-GLA-S1S3; M-052

Latest Information Update: 28 Mar 2025

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At a glance

  • Originator M6P Therapeutics
  • Class Gene therapies
  • Mechanism of Action Alpha-galactosidase replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No
  • Available For Licensing Yes

Highest Development Phases

  • No development reported Fabry's disease

Most Recent Events

  • 28 Mar 2025 No recent reports of development identified for preclinical development in Fabry's-disease in USA (Parenteral)
  • 09 Feb 2023 M6P Therapeutics plans to file IND for Fabry's disease by Q1 2025 (M6P Therapeutics website, February 2023)
  • 04 Feb 2021 M 052 is available for licensing as of 04 Feb 2021

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