VO 659
Alternative Names: VO 659Latest Information Update: 19 Sep 2024
At a glance
- Originator Vico Therapeutics
 - Class Antisense oligonucleotides
 - Mechanism of Action RNA modulators
 
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              Orphan Drug Status
              Yes - Spinocerebellar ataxias; Huntington's disease
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
 - New Molecular Entity Yes
 
Highest Development Phases
- Phase I/II Huntington's disease; Spinocerebellar ataxias
 
Most Recent Events
- 16 Sep 2024 Interim efficacy, adverse event and pharmacokinetic data from a phase I/II trial in Huntington's disease released by Vico Therapeutics
 - 03 Apr 2023 Phase-I/II clinical trials in Spinocerebellar ataxias, Huntington's disease (Parenteral)
 - 03 Apr 2023 Pharmacodynamics data from the preclinical study in Huntington's disease and Spinocerebellar degeneration released by Vico Therapeutics