Research programme: muscular dystrophy therapeutics - AUM LifeTech
Latest Information Update: 13 Apr 2023
At a glance
- Originator AUM LifeTech
- Developer AUM LifeTech; University of Pennsylvania
- Class Antisense oligonucleotides
- Mechanism of Action Gene silencing
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Duchenne muscular dystrophy
Most Recent Events
- 13 Apr 2023 Discontinued for Duchenne muscular dystrophy in USA (Parenteral) (AUM LifeTech pipeline; April 2023)