ETV GBA
Alternative Names: ETV-GBALatest Information Update: 01 Apr 2021
At a glance
- Originator Denali Therapeutics Inc
- Class Antiparkinsonians; Glucosidases; Recombinant fusion proteins
- Mechanism of Action Glucosylceramidase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Research Gaucher's disease; Parkinson's disease