JAG 101
Alternative Names: JAG-101Latest Information Update: 21 May 2022
At a glance
- Originator Jaguar Gene Therapy
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Galactosaemia
Most Recent Events
- 16 May 2022 Pharmacodynamics data from preclinical studies in mouse model and GALT-null rat model of Type 1 galactosemia presented at the 25th Annual Meeting of American Society of Gene and Cell Therapy (ASGCT-2022)
- 26 Feb 2021 Preclinical trials in Galactosaemia in USA (Parenteral), prior to February 2021 (Jaguar Gene Therapy Pipeline, March 2021)