JAG 201
Alternative Names: JAG-201Latest Information Update: 12 Jul 2024
At a glance
- Originator Broad Institute
- Developer Jaguar Gene Therapy
- Class Behavioural disorder therapies; Gene therapies
- Mechanism of Action Gene transference; SHANK3 protein replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Autistic disorder; Telomeric 22q13 Monosomy Syndrome
Most Recent Events
- 12 Jul 2024 JAG 201 receives Fast Track designation for Autistic disorder [Intraventricular,Injection] in USA before July 2024
- 10 Jul 2024 JAG 201 receives Fast Track designation for Telomeric 22q13 Monosomy Syndrome [Intraventricular,Injection] in USA before July 2024
- 10 Jul 2024 JAG 201 receives Rare Pediatric Disease designation for Telomeric 22q13 Monosomy Syndrome [Intraventricular,Injection] and Autistic disorder [Intraventricular,Injection] in USA before July 2024