TSHA 119
Alternative Names: TSHA-119Latest Information Update: 28 Apr 2025
At a glance
- Originator University of Texas Southwestern Medical Center
- Developer Taysha Gene Therapies
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported GM2 gangliosidoses
Most Recent Events
- 28 Apr 2025 No recent reports of development identified for preclinical development in GM2-gangliosidoses in USA (Parenteral, Injection)
- 11 May 2021 Taysha Gene Therapies announces intension to file IND (or) CTA for GM2 gangliosidoses in end of 2021
- 03 Mar 2021 Preclinical trials in GM2 gangliosidoses in USA (Parenteral) before March 2021