GPH 301 - LENZ Therapeutics
Alternative Names: GPH-301 - LENZ TherapeuticsLatest Information Update: 28 Apr 2025
At a glance
- Originator Graphite Bio
- Developer LENZ Therapeutics
- Class Gene therapies; Stem cell therapies
- Mechanism of Action Cell replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Gaucher's disease type I; Gaucher's disease type III
Most Recent Events
- 28 Apr 2025 No recent reports of development identified for preclinical development in Gaucher's disease type I in USA (Parenteral)
- 28 Apr 2025 No recent reports of development identified for preclinical development in Gaucher's disease type III in USA (Parenteral)
- 21 Mar 2024 LENZ Therapeutics has merged with Graphite Bio to form LENZ Therapeutics