Research programme: Ataxin 2 inhibitors - Maze Therapeutics
Alternative Names: Ataxin 2 inhibitors - Maze Therapeutics; ATXN2 programme - Maze TherapeuticsLatest Information Update: 29 Apr 2021
At a glance
- Originator Maze Therapeutics
- Class Gene therapies; RNA
- Mechanism of Action Ataxin-2 expression inhibitors; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Amyotrophic lateral sclerosis