Research programme: GalXC-plus siRNA therapeutics - Dicerna Pharmaceuticals
Alternative Names: GalXc-Plus Gen 2; GalXC-Plus-ALDH2; GaLXC-Plus-TUBB3; GaLXC-Plus-ß-tubulin IIILatest Information Update: 29 Dec 2021
At a glance
- Originator Dicerna Pharmaceuticals
- Class Amino sugars; Drug conjugates; Small interfering RNA
- Mechanism of Action Aldehyde dehydrogenase 2 modulators; Beta III tubulin protein modulators; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Neurological disorders