NRTX 1001
Alternative Names: GABA-secreting interneurons; NRTX-1001; NTX-001 - Neurona TherapeuticsLatest Information Update: 21 Jun 2024
At a glance
- Originator Neurona Therapeutics
- Class Pluripotent stem cell therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Partial epilepsies
Most Recent Events
- 18 Jun 2024 NRTX 1001 receives Regenerative Medicine Advanced Therapy (RMAT) status for Partial epilepsies in USA
- 14 Jun 2024 Neurona Therapeutics plans a phase I trial in Temporal lobe epilepsy (Treatment-resistant) (Intracerebral) (NCT06422923)
- 15 Apr 2024 Efficacy and adverse events data from a phase I/II trial in Partial epilepsies presented at the American Academy of Neurology 2024 Annual Meeting (AAN-2024)